AGAMREE Approval: What this means for you and your family

Ғылым және технология

PPMD was recently joined by Dr. Aravindhan Veerapandiyan of Arkansas Children’s Hospital to discuss the FDA’s recent approval of AGAMREE (vamorolone), a new steroid approved for the treatment of Duchenne muscular dystrophy in individuals aged 2 years and older.

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  • @jaysimoes3705
    @jaysimoes37058 ай бұрын

    Great info, I really feel that I am sceptical of the advantages for the kid. They sure seem to be there, but cushingoid syndrom and weight gain need to be dealt with in future medications for sure. But may be one step at the time. As far as I know, not all gene therapy require you to stay on steroids. SOme do, some don't but correct me if I am wrong.

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